Migalastat Hydrochloride

米加司他盐酸盐

Report date: 2022/08/29 20:00:24
NMEFirst In Class

Base Information

Drug NameMigalastat Hydrochloride
Drug Alias Name米加司他Amigal-ERT combo therapymigalastat-ERT combo therapyAmigalGalafold +[9
ClassificationSmall molecules > Heterocyclic drugs
Mechanisms of Actionα-Galactosidase stimulants
Targetsα-Galactosidase
Therapy Area/IndicationsFabry Disease
Global Approved IndicationsFabry Disease
Approved Indications in ChinaN/A
Original Approved Country/TerritoryEU
Original Approved Date2016/05/25
Country/TerritoryBelgiumCanadaUnited States +[20
CombinationsNo
Global Highest StatusApproved
Highest Status in ChinaN/A
Originator CompaniesAmicus Therapeutics Inc
China Registration ClassN/A

Develop Information

Inactive CompaniesN/A
Active IndicationsFabry Disease
Inactive IndicationsN/A

Other Information

ATC CodeA16AX