Cystic fibrosis gene therapy - CFTR-cationic lipid complex

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Report date: 2022/01/14 13:23:58

Base Information

Drug NameCystic fibrosis gene therapy - CFTR-cationic lipid complex
Drug Alias NameCFTR gene-cationic lipid complexCFTR gene-cytofectin complexCystic fibrosis gene therapy - CFTR-cytofectin complex
ClassificationCell and gene therapy > Gene therapy
Mechanisms of ActionCystic fibrosis transmembrane conductance regulator stimulantsGene transference
TargetsCystic fibrosis transmembrane conductance regulator
Therapy Area/IndicationsCystic Fibrosis
Global Approved IndicationsN/A
Approved Indications in ChinaN/A
Original Approved Country/TerritoryN/A
Original Approved DateN/A
Country/TerritoryN/A
CombinationsNo
Global Highest StatusDiscontinued (Phase 1 Clinical)
Highest Status in ChinaN/A
Originator CompaniesGenzyme Corp
China Registration ClassN/A

Develop Information

Active CompaniesN/A
Active IndicationsN/A
Inactive IndicationsCystic Fibrosis

Other Information

ATC CodeN/A
Related LinksN/A