rSIV.F/HN-CFTR (Boehringer-Ingelheim/UK Cystic Fibrosis Gene Therapy Consortium/Imperial College London/University of Edinburgh/University of Oxford)

N/A

报告时间: 2025/01/26 15:39:00

基本信息

药物名称rSIV.F/HN-CFTR (Boehringer-Ingelheim/UK Cystic Fibrosis Gene Therapy Consortium/Imperial College London/University of Edinburgh/University of Oxford)
药物别称CFTR gene therapy (Sendai virus vector/F/HN-type SIV vector) (Boehringer-Ingelheim/UK Cystic Fibrosis Gene Therapy Consortium/Imperial College London/University of Edinburgh/University of Oxford)lentiviral vector-based gene therapy (Boehringer-Ingelheim/UK Cystic Fibrosis Gene Therapy Consortium/Imperial College London/University of Edinburgh/University of Oxford)
药物类型生物药
作用机制囊性纤维化跨膜传导调节因子刺激剂
靶点囊性纤维化跨膜传导调节因子
治疗领域 / 适应症囊性纤维化
全球批准适应症N/A
中国批准适应症N/A
首批国家/区域N/A
首批日期N/A
国家/区域德国英国
是否复方
全球最高研发状态临床前
中国最高研发状态N/A
注册分类N/A

研发信息

非活跃公司N/A
活跃适应症囊性纤维化
非活跃适应症N/A

其他信息

ATC代码N/A
相关链接N/A