synthetic adeno-associated viral vector-based ASAH1 gene therapy (Gromit Therapeutics/Icahn School of Medicine/Hebrew University of Jerusalem)

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报告时间: 2025/01/26 15:53:58

基本信息

药物名称synthetic adeno-associated viral vector-based ASAH1 gene therapy (Gromit Therapeutics/Icahn School of Medicine/Hebrew University of Jerusalem)
药物别称ASAH1 gene therapy (Gromit Therapeutics/Icahn School of Medicine/Hebrew University of Jerusalem)Anc80L65 vector-based ASAH1 gene therapy (Gromit Therapeutics/Icahn School of Medicine/Hebrew University of Jerusalem)
药物类型生物药
作用机制酸性神经酰胺酶刺激剂
靶点酸性神经酰胺酶
治疗领域 / 适应症肺性高血压
全球批准适应症N/A
中国批准适应症N/A
首批国家/区域N/A
首批日期N/A
国家/区域美国以色列
是否复方
全球最高研发状态临床前
中国最高研发状态N/A
注册分类N/A

研发信息

非活跃公司N/A
活跃适应症肺性高血压
非活跃适应症N/A

其他信息

ATC代码N/A
相关链接N/A